- How does someone acquire (get) Duchenne Muscular Dystrophy? Is DMD inherited from a person’s
parents or do they get it from the environment? Explain.
- Who is more likely to acquire DMD, boys or girls? Why is that? Could a person have a mutated gene for
dystrophin but not have DMD? How?
- Genes include information used to make something in cells. What is supposed to happen with the
information on the gene for dystrophin and what happens when a person has a mutation of the gene?
- What is the function of dystrophin in muscles? How does a mutation
affect the function of dystrophin? - If we found a way to repair a single cell with the mutated gene for
dystrophin in a 2-year old child, could we cure DMD by repairing that single cell?
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